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UPDATE 1-Catalyst Pharma's neuromuscular drug succeeds in study
2017年3月15日 / 下午1点00分 / 8 个月前

UPDATE 1-Catalyst Pharma's neuromuscular drug succeeds in study

(Adds details, updates shares)

March 15 (Reuters) - Catalyst Pharmaceuticals Inc said on Wednesday its experimental drug to treat patients with a severe form of myasthenia gravis (MG), a rare neuromuscular disease, met the main goals of a study.

The drug, Firdapse, was being tested on seven patients with Musk-MG, a rare subpopulation of MG patients. There are currently no therapies for this form of MG approved by the U.S. Food and Drug Administration (FDA).

While several treatment options are available for MG, Musk-MG patients are typically resistant to them. Patients often face a lifetime of severe complications including difficulty walking, talking, swallowing and breathing normally.

Catalyst said it intends to discuss a plan with the FDA to take Firdapse into a pivotal study.

The drug, if approved, is likely to become the first-line standard of care for Musk-MG, the company said.

Firdapse is also being tested for Lambert-Eaton myasthenic syndrome, a rare and sometimes fatal autoimmune disease characterized by muscle weakness.

Catalyst’s shares jumped 17 percent to $1.37 before the bell on Wednesday. (Reporting by Divya Grover in Bengaluru; Editing by Savio D‘Souza and Sai Sachin Ravikumar)

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